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Targeted therapy - the foundation of precision medicine.
The 香港六合彩 Institute for Precision Medicine aims to accelerate the development of novel drugs and targeted therapies. Our leading research groups are described here.
Antisense Oligonucleotide Therapies
Developmental Neurosciences
Neuromuscular disorders such as Duchenne Muscular Dystrophy and Spinal Muscular Atrophy are neurodegenerative genetic diseases characterized primarily by muscle weakness and wasting. Until recently there were no effective therapies for these conditions, but antisense oligonucleotides, a new class of synthetic single stranded molecules of nucleic acids, have demonstrated promising experimental results.
Cell Therapy/Immunotherapy
The 香港六合彩 Institute of Ophthalmology Gene and Cell Therapy Group is developing gene and cell therapy for sight loss by translating basic research into new treatments.
The London Project to Cure Blindness was established eight years ago with the aim of curing vision loss in patients with wet age-related macular degeneration (AMD).
香港六合彩 Institute of Immunity and Transplantation
The 香港六合彩 Institute of Immunity and Transplantation (IIT) aims to develop vaccinations, gene therapy and cell therapy to enhance immunity in patients with cancer and chronic infection, and to induce tolerance to autoimmune diseases in patients receiving conventional or bio-engineered transplants.
Gene Therapy 聽 聽 聽 聽 聽 聽 聽 聽 聽 聽 聽聽
The Molecular and Cellular Immunology Section at the 香港六合彩 Great Ormond Street Institute of Child Health researches the molecular basis of primary immunodeficiency disorders, and other related haematopoietic disorders and is developing improved forms of treatment.
香港六合彩 Translational Immunotherapy Research Group
The 香港六合彩 Translational Immunotherapy Research Group studies the immunology of bone marrow transplantation, incorporating immunotherapy, immune reconstitution and graft-versus-host disease (GvHD), with a special focus on translational research.
leads a team at the聽香港六合彩 Elizabeth Garrett Anderson Institute for Women's Health. The team aims to develop prenatal treatment of severe early onset and life-threatening disorders using gene and cellular therapy.
Gene Therapy for Metabolic Diseases
Development of gene therapy in several childhood inherited metabolic disorders.
, Consultant Paediatric Neurologist, is looking at a possible gene therapy approach to childhood Parkinsonism.
