Gene therapy may cure rare diseases but drugmakers have few incentives
21 June 2024
"This is a massive challenge and I'm not entirely sure we're going to be able to overcome it, but we have to give it a go because we've spent decades making these transformative treatments," outlines Professor Claire Booth (Ïã¸ÛÁùºÏ²Ê Great Ormond Street Institute of Child Health).